It also reviews key players involved in the therapeutic development for Gaucher's Disease
and special features on late-stage and discontinued projects.
Companies involved in therapeutics development for Gaucher's Disease
and discussed in this research include Amicus Therapeutics, Inc.
Mitral valve prolapse and mitral insufficiency in two siblings with Gaucher's disease
Natural autoantibodies in sera of patients with Gaucher's disease
In the new study, the researchers revealed how the widely available prescription drugs diltiazem, verapamil, and in some cases dantrolene, acted on cells from patients with Gaucher's disease
Acute bilateral symmetrical pathologic fractures of the lateral tibial plateaus in a patient with Gaucher's disease
The recent arrival on the market of a modified glucocerebrosidase (Ceredase) for Gaucher's Disease
and last year's approval of PEG-adenosine deaminase for severe combined immunodeficiency disease illustrate the growing capabilities of the pharmaceutical industry to provide endogenous compounds that patients are lacking.
A snapshot of the global therapeutic scenario for Gaucher's Disease
Brady first proposed enzyme-replacement therapy for Gaucher's disease
25 years ago.
Tiscornia's project is entitled "Development of an induced pluripotent stem cell model of neuronopathic Gaucher's Disease
for investigating mechanisms of pathogenesis and small molecule testing.
, an inherited enzyme deficiency, affects more than 20,000 people in the United States and is especially prevalent among Jews of Eastern European ancestry.
Our clinical trial report, "Gaucher's Disease
Global Clinical Trials Review, H2, 2012" provides data on the Gaucher's Disease
clinical trial scenario.
Oxford GlycoSciences plc (LSE: OGS) today announced that OGT 918 (Vevesca(TM)) has been designated as an Orphan Medicinal Product by the European Commission for the treatment of Gaucher's Disease
The finding will improve genetic counselingfor victims of the the most serious forms of Gaucher's disease
, which is caused by the enzyme deficiency, report the researchers in the March 5 NEW ENGLAND JOURNAL OF MEDICINE.
Global Markets Direct's, 'Gaucher's Disease
- Pipeline Review, H1 2012', provides an overview of the Gaucher's Disease